Spinal Muscular Atrophy (SMA) Research and Clinical Hub UK
|Sponsor / Funder||Great Ormond Street Hospital|
|Funder||UK SMA charity: SMA TRUST|
|CI||Professor Francesco Muntoni|
|Sites||Newcastle, London GOSH|
This is a national clinical and research network for patients with SMA.
To provide a national agreement on
- clinical assessment
- physiotherapy assessment
- and treatment for SMA patients
We propose designing, piloting and expanding an electronic database. The database will streamline the collection of data for SMA patients.
The UK SMA database, a unique infrastructure, will be developed at GOSH and Newcastle. It will soon be built up and accessible to specialist centres treating SMA patients across the UK.