Close
Clinical Trial of Investigational Medicinal Products (CTIMP)
- GSK Extension study (DMD)
- Restoring dystrophin (DMD)
- AVI-4658 (DMD)
- PRO051 - GSK2402968 (DMD)
- SMT C1100 (DMD)
- PTC124 (Duchenne and Becker muscular dystrophy)
- Arimoclomol (IBM)
- Mexiletine (Non-dystrophic myotonia)
- HYP HOP study (Dichlorphenamide for Periodic Paralysis)
- Olesoxime (TRO19622) (SMA)
Cohorts
- Complication of pregnancy (Mitochondrial disease)
- Jain Foundation limb-girdle muscular dystrophy type 2B
- Outcome measure in SMA type II and III
- OPTIMISTIC (Myotonic Dystrophy)
- Genotype - phenotype correlation and longitudinal studies (Non-dystrophic Myotonias)
- Genotype - phenotype correlation and longitudinal studies (Andersen-Tawil syndrome)
- Genotype - phenotype correlation and longitudinal studies (Episodic Ataxia Syndrome)