Biomedical research
Biomedical Sciences

Biomedical research

Understanding the role of the interruptions in repeat expansion diseases, Preclinical testing of ataxia therapies, Mitochondrial pathophysiology in rare disorders

Clinical Studies (Observational and Biomarkers studies)
neurons

Clinical Studies (Observational and Biomarkers studies)

Observational clinical studies are vitally important to our understanding of the causes and natural course of movement disorders, improving care options and identifying new therapeutic targets.

Clinical Trials (drug and treatment trials)
lab worker

Clinical Trials (drug and treatment trials)

Interventional clinical trials ("drug trials") test the safety and efficacy of new drugs and treatments that could potentially help manage symptoms better or even slow or halt disease progression.

Research registries
paper graphic

Research registries

There are various research registries available on the different types of ataxias, some are clinical reported registries, and others are registries with patient reported information.