Stem Cell News

First targeted treatment success for Duchenne Muscular Dystrophy

25 July 2011

A team of UCL scientists, funded by the Medical Research Council and AVI BioPharma, together with the MDEX Consortium, chaired by UCL Professor Francesco Muntoni, show in a paper published in The Lancet today that a gene-based drug treatment was effective in restoring the dystrophin protein that is missing in sufferers of Duchenne Muscular Dystrophy , in 7 out of 19 trial participants.

Tom and James Bosanquet More at UCL News

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