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Gene and Cell Therapy Group
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In the newsPhotoreceptor transplants restore vision in mice Europe's first stem cell trial: Stargardt disease |
Developing gene and cell therapy for sight loss by translating basic research into new treatments
We are currently conducting two ground-breaking clinical trials:
The world's first gene therapy trial in the eye, testing the safety and efficacy of delivering the RPE65 gene to patients with Leber congenital amaurosis (LCA).More >> |
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Europe's first trial testing the safety of transplanting stem cell-derived retinal cells into the eyes of patients with Stargardt diseaseMore >> |
Research highlights
Stem cell transplants restore vision in mice
Two recent studies from our group, published in Nature and Proceedings of the National Academy of Sciences, show that transplanted photoreceptor cells can restore vision in models of sight loss.
Key achievements
The world's first eye gene therapy trial - JWB Bainbridge et al. N Engl J Med. 2008
Cell therapy repairs the retina - Pearson RA et al Nature 2012
The first proof-of-concept in eye gene therapy - RR Ali et al. Nat. Genet. 2000
Our latest blog posts
It’s OK to ask about clinical research – an NIHR campaign
‘Defining future eye research’ – a chance for you to help tackle slight loss
EyeTherapy information hub
Visit the EyeTherapy information hub for an in-depth look at our research, and the EyeTherapy blog for updates, newsletter and more
Page last modified on 13 feb 13 14:23
