UCL Great Ormond Street Institute of Child Health


Duchenne muscular dystrophy and clinical trials

When Emma’s son Sam was three he was diagnosed with Duchenne muscular dystrophy (DMD), a life-limiting condition which causes the breakdown and loss of muscle cells. Here, Emma shares her experience of having a child with DMD, and what it’s like to take part in a clinical trial at Great Ormond Street Hospital (GOSH).

If you want to read the full interview visit the GOSH website